Familial amyloid polyneuropathy, also called transthyretin-related hereditary amyloidosis, transthyretin amyloidosis abbreviated also as ATTR (hereditary...
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Neuromuscular Group) (April 2020). "Pharmacological treatment for familial amyloid polyneuropathy". The Cochrane Database of Systematic Reviews. 4 (4): CD012395...
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The familial amyloid neuropathies (or familial amyloidotic neuropathies, neuropathic heredofamilial amyloidosis, familial amyloid polyneuropathy) are a...
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be used to treat both hereditary forms, familial amyloid cardiomyopathy and familial amyloid polyneuropathy, as well as wild-type transthyretin amyloidosis...
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only a few cases are familial. Others are only familial. Some result from medical treatment. Prions are an infectious form of amyloids that can act as a...
60 KB (6,536 words) - 06:48, 29 August 2024
Familial amyloid cardiomyopathy (FAC), or transthyretin amyloid cardiomyopathy (ATTR-CM) results from the aggregation and deposition of mutant and wild-type...
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associated with amyloid diseases including wild-type transthyretin amyloidosis, hereditary transthyretin amyloidosis, familial amyloid polyneuropathy (FAP), and...
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(April 2008). "Marked regression of abdominal fat amyloid in patients with familial amyloid polyneuropathy during long-term follow-up after liver transplantation"...
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Transthyretin-Mediated Amyloid Polyneuropathy" at ClinicalTrials.gov Clinical trial number NCT01737398 for "Efficacy and Safety of Inotersen in Familial Amyloid Polyneuropathy"...
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(Vyndaqel, Vyndamax) Transthyretin chaperone (stabilizer) Familial amyloid polyneuropathy and other transthyretin amyloidoses 2011 2019 Voxelotor (Oxbryta)...
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