Familial amyloid polyneuropathy, also called transthyretin-related hereditary amyloidosis, transthyretin amyloidosis abbreviated also as ATTR (hereditary...

Neuromuscular Group) (April 2020). "Pharmacological treatment for familial amyloid polyneuropathy". The Cochrane Database of Systematic Reviews. 4 (4): CD012395...

The familial amyloid neuropathies (or familial amyloidotic neuropathies, neuropathic heredofamilial amyloidosis, familial amyloid polyneuropathy) are a...

Familial amyloid cardiomyopathy (FAC), or transthyretin amyloid cardiomyopathy (ATTR-CM) results from the aggregation and deposition of mutant and wild-type...

only a few cases are familial. Others are only familial. Some result from medical treatment. Prions are an infectious form of amyloids that can act as a...

be used to treat both hereditary forms, familial amyloid cardiomyopathy and familial amyloid polyneuropathy, as well as wild-type transthyretin amyloidosis...

associated with amyloid diseases including wild-type transthyretin amyloidosis, hereditary transthyretin amyloidosis, familial amyloid polyneuropathy (FAP), and...

(April 2008). "Marked regression of abdominal fat amyloid in patients with familial amyloid polyneuropathy during long-term follow-up after liver transplantation"...

Transthyretin-Mediated Amyloid Polyneuropathy" at ClinicalTrials.gov Clinical trial number NCT01737398 for "Efficacy and Safety of Inotersen in Familial Amyloid Polyneuropathy"...

(Vyndaqel, Vyndamax) Transthyretin chaperone (stabilizer) Familial amyloid polyneuropathy and other transthyretin amyloidoses 2011 2019 Voxelotor (Oxbryta)...